In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers.
Chen M, Shi H, Gou S, Wang X, Li L, Jin Q, Wu H, Zhang H, Li Y, Wang L, Li H, Lin J, Guo W, Jiang Z, Yang X, Xu A, Zhu Y, Zhang C, Lai L, Li X.
Chen M, et al. Among authors: li y, li h, li x, li l.
Genome Med. 2021 Apr 12;13(1):57. doi: 10.1186/s13073-021-00876-0.
Genome Med. 2021.
PMID: 33845891
Free PMC article.